Neuren Reports Results for NNZ-2591 in P-II Trial for the Treatment of Children with Phelan-McDermid Syndrome (PMS)
Shots:
- The P-II trial evaluates NNZ-2591 (oral liquid dose, BID) in 20 children (aged 3-12yrs.) with PMS for 13wks. followed by an assessment post 2wks. of treatment. The 1EPs of the study include safety, tolerability & PK & 2EPs include 14 efficacy measures assessed by clinicians (CGI-I) & caregivers (CIC)
- As per the safety results, NNZ-2591 was well tolerated & efficacy data showed a significant improvement from baseline for 10/14 endpoints. Of 18 evaluable patients, 16 & 15 depicted improvements measured by CGI-I & CIC with mean scores 2.4 & 2.7 respectively
- The company is also conducting a P-II trial for NNZ-2591 in children with Pitt-Hopkins syndrome (results expected by Q2'24), Angelman syndrome & Prader-Willi syndrome
Ref: PR Newswire | Image: Neuren
Related News:- Acadia Expands its License Agreement with Neuren to Acquire Ex-North American Rights to Trofinetide and Global Rights to NNZ-2591
PharmaShots! Your go-to media platform for customized news ranging for multiple indications. For more information connect with us at connect@pharmashots.com
Click here to read the full press release
Tags
Kritika is a content writer at PharmaShots. She is interested in covering recent innovations from the pharma & MedTech industry. She covers news related to Product approvals, clinical trial results, and updates. She can be contacted at connect@pharmashots.com.
